Faculty Research 1990 - 1999
Two-hit model for sporadic congenital anomalies in mice with the disorganization mutation.
Document Type
Article
Publication Date
1993
Keywords
Animal, Chi-Square-Distribution, Chromosome-Abnormalities: ge, Disease-Models-Animal, Gene-Expression, Genes-Dominant, Mice, Mice-Inbred-Strains, Mice-Mutant-Strains: ge, Models-Genetic, Mutation, Poisson-Distribution, SUPPORT-U-S-GOVT-P-H-S
First Page
866
Last Page
874
JAX Source
Am J Hum Genet 1993 May;52(5):866-74
Grant
HD25389/HD/NICHD
Abstract
Congenital anomalies have complex etiologies involving both genetic and nongenetic components. Many are sporadic, without obvious evidence for heritability. An important model for these anomalies is a mutation in laboratory mice that is called "disorganization" (Ds), which functions as a variable autosomal dominant and leads to a wide variety of congenital anomalies involving many developmental processes and systems. Variable expressivity, asymmetrical manifestations, and low penetrance suggest that somatic events determine the location and nature of these anomalies. A statistical analysis suggests that occurrence of anomalies in mice with the Ds mutation follows a Poisson distribution. These results suggest that congenital anomalies in mice with the Ds mutation occur independently of each other. We propose that Ds causes a heritable predisposition to congenital anomalies and that Ds and appropriate somatic events combine to compromise normal development. We also propose that some sporadic, nonheritable congenital anomalies involve somatic mutations at Ds-like loci. Ds may therefore serve not only as a model for developmental anomalies in cell fate and pattern formation but also for complex developmental traits showing variable expressivity, low penetrance, and sporadic occurrence in mice and humans.
Recommended Citation
Crosby JL,
Varnum DS,
Nadeau JH.
Two-hit model for sporadic congenital anomalies in mice with the disorganization mutation. Am J Hum Genet 1993 May;52(5):866-74